Gene Therapy Review
Welcome to our gene therapy portal
The Gene Therapy Review is the web resource for patients and professionals interested in cell and gene therapy. Founded in 2008, the aim of the site is to be an information resource for basic and clinical research in the fields of gene therapy, cell therapy, and genetic vaccines, and to serve as a network in the exchange of information and news related to this arena. We welcome contributions from researchers and clinicians alike with a view in increase awareness in this vastly growing sector.
Gene Therapy in the News
Compared with direct gene injection, cell-mediated GDNF gene delivery led to considerably more pronounced preservation of myelinated fibers in the remote segments of the spinal cord (5 vs 3 mm from the epicenter), and this might depend on the expansion of the therapeutic influence in cell-mediated therapy over long distances as a result of the migration of the transplanted cells.
Mutations in DNMT3A gene cause MEIS1 activacion, triggering leukemia, a research team demonstrates.
A novel mouse model for the vision disorder Leber hereditary optic neuropathy (LHON) has been developed by researchers who have found that they can use gene therapy to improve visual function in the mice. LHON is one of many diseases tied to gene mutations that damage the tiny energy factories that power our cells, called mitochondria.